What gene therapies are approved?
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Simply so, are there any approved gene therapies?
The U.S. Food and Drug Administration (FDA) has approved only a limited number of gene therapy products for sale in the United States. Hundreds of research studies (clinical trials) are under way to test gene therapy as a treatment for genetic conditions, cancer, and HIV/AIDS.
Secondly, what is an example of gene therapy? Gene therapy is the introduction of genes into existing cells to prevent or cure a wide range of diseases. For example, suppose a brain tumor is forming by rapidly dividing cancer cells. The other target of some of the various retroviruses used include: bone marrow, skin, and liver cells.
Likewise, how many gene therapies are approved?
At least nine gene therapies have been approved for certain kinds of cancer, some viral infections and a few inherited disorders.
What is the world first approved gene therapy product by a regulatory agency?
In December, the FDA approved Luxturna, the first in vivo gene therapy, for the treatment of blindness due to Leber's congenital amaurosis.